CRISPR/cas9基因编辑通过两种导向RNA,分别为5'-GTCGCCGCTAGCCTGG-3'和5'-GATTTGGAGATTCAGGC-3',靶向基因的第1和2外显子。 Western blot结果显示没有检测到蛋白质。(来源:J:335286)
Legend:
cx: complex: > 1 genome feature ot: other: hemizygous, indeterminate,... (F): Female
(M): Male
N: normal phenotype
(#): related diseases count