Ins2基因的GG2-GG1/A2-C1增强子区域通过CRISPR/Cas9技术,用sgRNAs针对CTTTCTGCAGACCTAGCACCAGG和AAACTGCAGCTTCAGCCCCTCTGG这两个靶点进行了编辑,产生了C1元素上的1个碱基缺失(替换为C)。(来源:J:312429)
Legend:
cx: complex: > 1 genome feature ot: other: hemizygous, indeterminate,... (F): Female
(M): Male
N: normal phenotype
(#): related diseases count