CRISPR/Cas9 methodologies were used to introduce a 1 bp base pair mutation (C>T) resulting in a H71Y point mutation. The mutation is associated with Amyotrophic Lateral Scleroris. (J:101977)
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CRISPR/Cas9 methodologies were used to introduce a 1 bp base pair mutation (C>T) resulting in a H71Y point mutation. The mutation is associated with Amyotrophic Lateral Scleroris. (J:101977)